Sapropterin
| Full Name | Sapropterin |
| Drug | sapropterin dihydrochloride |
| Manufacturer | Generic |
| Route of Administration | Oral |
| Site of Care | Home |
| Approved Indication | Reduce blood phenylalanine (Phe) levels in adult and pediatric patients one month of age and older with hyperphenylalaninemia (HPA) due to tetrahydrobiopterin- (BH4-) responsive Phenylketonuria (PKU), in conjunction with a Phe-restricted diet |
| Disease | Phenylketonuria (PKU) |
| Therapeutic Area | Endocrinology |
| Enrollment Form Link | Enrollment Form |
| Phone Number | (773) 598-6135 |
| Fax Number | (877) 299-8203 |
| Patient Resources | Alliance of PKU Families, flok, and National PKU Alliance |