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Sapropterin

 

Full Name Sapropterin
Drug sapropterin dihydrochloride
Manufacturer Generic
Route of Administration Oral
Site of Care Home
Approved Indication Reduce blood phenylalanine (Phe) levels in adult and pediatric patients one month of age and older with hyperphenylalaninemia (HPA) due to tetrahydrobiopterin- (BH4-) responsive Phenylketonuria (PKU), in conjunction with a Phe-restricted diet
Disease Phenylketonuria (PKU)
Therapeutic Area Endocrinology
Enrollment Form Link Enrollment Form
Phone Number (773) 598-6135
Fax Number (877) 299-8203
Patient Resources National PKU Alliance