Vyondys 53® (golodirsen)
| Full Name | Vyondys 53® (golodirsen) |
| Drug | Vyondys 53 |
| Manufacturer | Sarepta Therapeutics, Inc. |
| Route of Administration | Intravenous |
| Site of Care | Home or Healthcare Facility |
| Approved Indication | The treatment of Duchenne muscular dystrophy (DMD) in patients who have a confirmed mutation of the DMD gene that is amenable to exon 53 skipping |
| Disease | Duchenne Muscular Dystrophy (DMD) |
| Therapeutic Area | Neurology |
| Enrollment Form Link | Vyondys 53 Enrollment Form |
| Phone Number | 800-356-5034 |
| Fax Number | 877-339-4602 |
| Product Website | vyondys53.com |
| Patient Resources | Alex Rezcalla Foundation, Jett Foundation, Muscular Dystrophy Association, and Parent Project Muscular Dystrophy |